The gains of scientific advancements in treatment are shadowed by the cuts coming in Medicaid coverage at rare disease fair.
Patients, doctors and legislators spoke about the struggles of those with rare diseases.
Four-day global conference will spotlight emerging therapies, artificial intelligence, genetic medicine, clinical trial ...
Breast cancer is the most common form of cancer in the UK but is rare in younger women. Women in their 20s accounted for only ...
Trey Robertson has long struggled with sickle cell but has tried not to let that slow him down — and he encourages others to ...
Gene therapy cut severe infections 93% in Wiskott-Aldrich syndrome, using patients’ own modified stem cells to treat a rare ...