A new bipartisan bill aims to speed rare disease drug development by making clinical trials faster, cheaper and more ...

AstraZeneca said it received U.S. approval for its Ultomiris drug as a treatment for foamy urine in adults with immunoglobulin A nephropathy, a rare condition that can lead to chronic kidney disease.

More than 41 million people are living with HIV worldwide, and approximately 570,000 died from AIDS-related illnesses in 2025 ...

Biomarker results support previously reported functional (LCVA) +18-letter gains and structural retinal preservation at Month ...

Vanderbilt Health researchers have created a “map” of 1,757 genetic variations that can trigger a life-threatening heart rhythm disorder called long QT syndrome.

DuPage County Health Department says a vaccinated county resident recently returned from international travel has contracted ...

Scientists put their stamps on medical-science history by naming their discoveries. Those names have serious scientific implications.

Health officials have confirmed DuPage County’s first measles infection of the year in a resident who was vaccinated against ...

(NASDAQ: SCYX) (“SCYNEXIS” or the “Company”), a clinical-stage biotechnology company dedicated to advancing innovative solutions for severe rare diseases, announces that SCY-247, its second-generation ...

Where Rare-Disease Treatments Stall Some promising treatments for rare childhood diseases face significant funding gaps before they can reach clinical... Read More ...

Proposed collaboration covers scientific exchange, specialist training and real-world evidence, alongside assessment of ...

The NHS has confirmed a change with patients who have cancer and heart disease set to benefit. The Labour Party government, ...