Gene therapy is no longer the future of medicine—it's reality. Treatments that replace, silence or edit genes are already ...

Gene by Gene, a leading genomics laboratory specializing in high-throughput sequencing and precision medicine, today announced a research collaboration with Children's Mercy to provide Whole Genome ...

Foundation will present the first data from its LGS Collaborative Outcomes Registry (LGS-CORE) at the 2026 NORD Rare Diseases & Orphan Products Breakthrough Summit, October 25 to 27 in Washington, DC.

From cancer and epilepsy to autoimmune and neurological disorders, these 10 Bollywood celebrities faced serious health battles and inspired millions through resilience, treatment, and recovery.

Doctors in Mumbai have successfully treated a newborn diagnosed with Cantrell`s Pentalogy, an exceptionally rare congenital ...

GeneDx (Nasdaq: WGS), the leader in rare disease diagnosis and improving health through the power of genomic data, today announced plans to enhance its genome testing portfolio with long-read whole ...

This requires more than individual breakthroughs. Notre Dame is investing $275 million in assembling new high-impact, ...

Eloxx Pharmaceuticals, Inc. (Nasdaq: ELOX), a clinical-stage biopharmaceutical company developing exaluren for the treatment of rare kidney diseases, today announced the finalized design of its ...

Oral olorofim was non-inferior to AmBisome® followed by standard of care (AmBisome®+SOC), with Day 42 all-cause mortality of 23.8% for olorofim ...

Edge Computational Medicine Platform to Build Core Infrastructure for the Life World Model. This innovative computational ...

The Pharmaceutical and Healthcare Association of the Philippines (PHAP) has reaffirmed its commitment to work closely with ...